Release Details
PTC Therapeutics Announces Five Winners In Its First-ever Global Duchenne Muscular Dystrophy Patient Group Award
"We are thrilled to present our STRIVE Awards to these organizations who are deeply passionate about making a positive difference in the lives of boys and young men affected by Duchenne muscular dystrophy," said
The impact of the STRIVE Awards will be felt around the world with awards granted to patient organizations in
|
|
|
|
|
|
|
|
|
Parent Project Muscular Dystrophy will create a campaign for healthcare professionals and at-risk women to raise awareness about carrier issues in the DMD community |
For complete information about STRIVE and each award recipient, please visit the STRIVE website at: http://www.ptcbio.com/en/about-ptc/ptc-strive-awards-program/
DMD is a rare genetic disorder that results in progressive muscle weakness from early childhood with subsequent loss of lower and then upper body function, leading to loss of the ability to walk at around 12 years of age. The STRIVE Awards recognize the vital role patient advocacy groups play in giving a voice to individuals affected by DMD, with the ultimate goal of facilitating unique, inventive ideas, methods or programs supporting patients and families within the DMD community. Award entries were received from 27 organizations from across 19 countries.
This awards program was established to support initiatives that will benefit the DMD community by increasing awareness, diagnosis and education, and fostering the development of future patient advocates. An independent panel of external experts with knowledge in rare diseases, patient advocacy and funding initiatives judged entries for feasibility, creativity, budget, impact and sustainability. Five one-year awards of
"We have a tremendous amount of respect for the important services and programs provided by these organizations for the Duchenne muscular dystrophy community," said
About Duchenne Muscular Dystrophy (DMD)
Primarily affecting males, Duchenne muscular dystrophy (DMD) is a progressive muscle disorder caused by the lack of functional dystrophin protein. Dystrophin is critical to the structural stability of skeletal, diaphragm, and heart muscles. Patients with DMD, the more severe form of the disorder, lose the ability to walk as early as age 10 and experience life-threatening lung and heart complications in their late teens and twenties. More information about DMD is available through the
About
PTC is a global biopharmaceutical company focused on the discovery, development and commercialization of orally administered, proprietary small molecule drugs targeting an area of RNA biology we refer to as post-transcriptional control. Post-transcriptional control processes are the regulatory events that occur in cells during and after a messenger RNA is copied from DNA through the transcription process. PTC's internally discovered pipeline addresses multiple therapeutic areas, including rare disorders, oncology and infectious diseases. PTC has discovered all of its compounds currently under development using its proprietary technologies. PTC plans to continue to develop these compounds both on its own and through selective collaboration arrangements with leading pharmaceutical and
biotechnology companies. For more information on the company, please visit our website www.ptcbio.com.
FOR MORE INFORMATION:
Investors:
+1(908) 912-9327
ehill@ptcbio.com
Media:
+1 (908) 912-9167
jbaj@ptcbio.com
To view the original version on PR Newswire, visit:http://www.prnewswire.com/news-releases/ptc-therapeutics-announces-five-winners-in-its-first-ever-global-duchenne-muscular-dystrophy-patient-group-award-300137943.html
SOURCE
News Provided by Acquire Media